Category: rare disease

New Imaging Protocol Could Vastly Accelerate Clinical Trials for New ALS Treatments

Researchers at Massachusetts General Hospital have developed a new technique for imaging the brains of patients with amyotrophic lateral sclerosis (ALS) that could vastly reduce the cost and time needed for new clinical trials—while also improving the accuracy of test results. Nazem Atassi, MD, the Associate Director of the Neurological Clinical Research Institute (NCRI) at ...

Genetic Insights, New Research Models Help to Drive New Rare Disease Research

While it may not have been called rare disease research by name, Massachusetts General Hospital has been identifying and tracking rare diseases for more than a century, says Florian Eichler, MD, Director of the Center for Rare Neurological Diseases in the Department of Neurology. In recent years, advances made by the Human Genome Project and ...